Autopsy report · NCT03853876

A Natural History Study of Aspartylglucosaminuria

“Discontinued AGU development program”

The sponsor’s own words in the registry.

Life of this trial

• Registered 3 months before it started.
• Ran for about 2 years 11 months before it stopped.
• 8 participants enrolled.
• No results are posted on the registry.

Vital statistics

Status

Terminated

Sponsor

Neurogene Inc.

Sponsor type

Industry

Conditions

Aspartylglucosaminuria; Aspartylglucosamidase (AGA) Deficiency; Lysosomal Storage Diseases

Participants

8

Sites

1

Countries

United States

Trials that died the same way

• A Randomized Double Blind, Placebo Controlled Trial With AMG 108 in Patients With Type 2 Diabetes Mellitus
  “Program Development discontinued” (66% match in meaning)
• Phase 1 Study of Shattuck Labs (SL)-172154 in Subjects With MDS or AML
  “Development discontinued” (61% match in meaning)

Look deeper

• The official registry record (the source of truth)
• Record history: every change the sponsor made
• Open it in the database

Everything here comes from the current ClinicalTrials.gov record. The timeline uses the record’s dates; dates marked planned are the sponsor’s plans. The cause of death is an automatic, unverified label. This is research information, not medical advice.